A novel lentivector targets gene transfer into hHSC in marrow from patients with BM- failure-syndrome and in vivo in humanized mice
نویسندگان
چکیده
Affiliation: Université de Lyon, F69007; Inserm, EVIR, U758, Human Virology Department, F-69007; Ecole Normale Supérieure de Lyon, F-69007; Université Lyon 1, F-69007, Lyon, France School of Life Sciences, Ecole polytechnique Féderale de Lausanne (EPFL), 1015 Lausanne, Switzerland Hematopoiesis and Gene Therapy Division, Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas and Centro de Investigación Biomédica en Red de Enfermedades Raras, Madrid, Spain. These author equally contributed to this work Co-corresponding authors
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